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Investigating Patients with Diffuse Large B-Cell Lymphoma Not Undergoing Stem Cell Transplant

Diffuse large B-cell lymphomas (DLBCL) are frequently cured after first-line treatment with rituximab plus cyclophosphamide, doxorubicin, vincristine, and prednisone (R-CHOP). In patients...

Defining Clinical and Economic Characteristics Among Male Patients with Rett Syndrome

According to T. Davis, PhD, very few studies have been conducted to describe the clinical and economic characteristics of male patients who...

Prescriptions Medications Used Before Diagnosis in Patients with Myotonic Dystrophy

Myotonic dystrophy (DM) is a rare, multisystem disease that causes myotonia, progressive muscle weakness, atrophy, and central nervous system dysfunction, and significantly...

Evaluating the Impact of Increased FDA Drug Approvals Based on Single-Arm Clinical Trials

Results from randomized controlled trials (RCTs) are the standard in formulary planning and clinical decision-making; however, the focus on rare disease in...
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